Hemophilia Gene Therapy: A New Hope for Patients

April 18, 2025

Hemophilia gene therapy represents a groundbreaking advancement in the treatment of this hereditary bleeding disorder.For patients like Terence Blue, who recently received Hemgenix at Brigham and Women’s Hospital, the hope is that this innovative approach will reduce reliance on traditional hemophilia treatment options, such as frequent clotting factor injections.
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